EMBRYONIC DEVELOPMENT & STEM CELL COMPENDIUM
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Muscular Dystrophy, Duchenne Type
 - Cell Therapy Approaches

Duchenne muscular dystrophy is caused by a mutation in the DMD gene, which encodes dystrophin, an important structural component of muscle tissue that provides structural stability to the dystroglycan complex (DGC) of the cell membrane. 

Cell Therapy Approaches


Cell therapy utilizing different stem cells have the potential to fuse with human myoblasts and to restore dystrophin expression.

Muscular Dystrophy, Duchenne Type